References
-
1.
Goncalves GAR, Paiva RMA. Gene therapy: advances, challenges and perspectives. Einstein (Sao Paulo). 2017;15(3):369-75. [PubMed ID: 29091160]. [PubMed Central ID: PMC5823056]. https://doi.org/10.1590/S1679-45082017RB4024.
-
2.
Kaufmann KB, Buning H, Galy A, Schambach A, Grez M. Gene therapy on the move. EMBO Mol Med. 2013;5(11):1642-61. [PubMed ID: 24106209]. [PubMed Central ID: PMC3840483]. https://doi.org/10.1002/emmm.201202287.
-
3.
Fraldi A, Serafini M, Sorrentino NC, Gentner B, Aiuti A, Bernardo ME. Gene therapy for mucopolysaccharidoses: in vivo and ex vivo approaches. Ital J Pediatr. 2018;44(Suppl 2):145-54. [PubMed ID: 30442177]. [PubMed Central ID: PMC6238250]. https://doi.org/10.1186/s13052-018-0565-y.
-
4.
Wolf DP, Mitalipov PA, Mitalipov SM. Principles of and strategies for germline gene therapy. Nat Med. 2019;25(6):890-7. [PubMed ID: 31160821]. https://doi.org/10.1038/s41591-019-0473-8.
-
5.
Chellappan DK, Sivam NS, Teoh KX, Leong WP, Fui TZ, Chooi K, et al. Gene therapy and type 1 diabetes mellitus. Biomed Pharmacother. 2018;108:1188-200. [PubMed ID: 30372820]. https://doi.org/10.1016/j.biopha.2018.09.138.
-
6.
Rosenberg SA, Aebersold P, Cornetta K, Kasid A, Morgan RA, Moen R, et al. Gene transfer into humans--immunotherapy of patients with advanced melanoma, using tumor-infiltrating lymphocytes modified by retroviral gene transduction. N Engl J Med. 1990;323(9):570-8. [PubMed ID: 2381442]. https://doi.org/10.1056/NEJM199008303230904.
-
7.
Kumaran N, Michaelides M, Smith AJ, Ali RR, Bainbridge JWB. Retinal gene therapy. Br Med Bull. 2018;126(1):13-25. [PubMed ID: 29506236]. https://doi.org/10.1093/bmb/ldy005.
-
8.
Rao P, Cozar-Castellano I, Roccisana J, Vasavada RC, Garcia-Ocana A. Hepatocyte growth factor gene therapy for islet transplantation. Expert Opin Biol Ther. 2004;4(4):507-18. [PubMed ID: 15102600]. https://doi.org/10.1517/14712598.4.4.507.
-
9.
Belete TM. The Current Status of Gene Therapy for the Treatment of Cancer. Biologics. 2021;15:67-77. [PubMed ID: 33776419]. [PubMed Central ID: PMC7987258]. https://doi.org/10.2147/BTT.S302095.
-
10.
Montano-Samaniego M, Bravo-Estupinan DM, Mendez-Guerrero O, Alarcon-Hernandez E, Ibanez-Hernandez M. Strategies for Targeting Gene Therapy in Cancer Cells With Tumor-Specific Promoters. Front Oncol. 2020;10:2671. [PubMed ID: 33381459]. [PubMed Central ID: PMC7768042]. https://doi.org/10.3389/fonc.2020.605380.
-
11.
Axelsen TM, Woldbye DPD. Gene Therapy for Parkinson's Disease, An Update. J Parkinsons Dis. 2018;8(2):195-215. [PubMed ID: 29710735]. [PubMed Central ID: PMC6027861]. https://doi.org/10.3233/JPD-181331.
-
12.
Eberling JL, Jagust WJ, Christine CW, Starr P, Larson P, Bankiewicz KS, et al. Results from a phase I safety trial of hAADC gene therapy for Parkinson disease. Neurology. 2008;70(21):1980-3. [PubMed ID: 18401019]. https://doi.org/10.1212/01.wnl.0000312381.29287.ff.